Our Research

The Gene Therapy Institute brings together a vibrant and dynamic community that fosters a collaborative approach to address the unique clinical challenges of gene therapy research, vector development & production, device & delivery engineering, operational efficiency, physician training and innovative business models to ensure maximal patient benefit.

Research Areas

Image of neurons
Nervous System Diseases
nanocarrier uptake by cells
Non-Viral Therapies
Image of Dr. Yanhui Ma reviewing images on computer

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A gift to the Gene Therapy Institute can take us closer to new discoveries and life-changing treatments.