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Our Research
The Gene Therapy Institute brings together a vibrant and dynamic community that fosters a collaborative approach to address the unique clinical challenges of gene therapy research, vector development & production, device & delivery engineering, operational efficiency, physician training and innovative business models to ensure maximal patient benefit.
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The Gene Therapy Institute is truly trans-institutional and designed to accelerate basic science discoveries into clinical cures for untreatable, or incompletely treated, disorders.
Support the Institute
A gift to the Gene Therapy Institute can take us closer to new discoveries and life-changing treatments.