Gene Therapy Institute

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Our Vision

The Gene Therapy Institute will be a world leader in gene therapy research, training and clinical care.
About Us
DNA strand artwork

The Gene Therapy Institute is an interdisciplinary community bringing together world-class faculty with diverse expertise in the area of gene therapy research. Through collaboration we are enabling the successful translation of basic science discoveries into new therapies that are accessible to affected populations around the globe. 

  • 18+ Innovative industry-partnerships
  • 50+ Faculty across 7 OSU colleges
  • $12.4M NIH funding awarded in FY2024

Gene Therapy Institute News

Dr. Mendel in the lab with a pipet

Foundation Fighting Blindness invests in adjuvant-assisted retinal gene therapy research

“Our focus is different,” Dr. Mendel says. “We use a gene agnostic surgical approach that ultimately could be used to deliver gene-specific therapy to patients with molecularly different types of inherited retinal disease.”
January 10, 2025
Dr. Stephen Kolb speaking to a small group of staff members

With compassion and curiosity, researcher is driven to slow ALS progression

Dr. Stephen Kolb brings hope against an incurable genetic disease to his patients.
May 21, 2024
Skeletal image of spine

Gene therapy relieves back pain, repairs damaged disc in mice

Disc-related back pain may one day meet its therapeutic match: gene therapy delivered by naturally derived nanocarriers that, a new study shows, repairs damaged discs in the spine and lowers pain symptoms in mice.
May 16, 2024

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